Prevention of dystrophic pathology in severely affected dystrophin/utrophin-deficient mice by morpholino-oligomer-mediated exon-skipping

Molecular Therapy (2010) - Comments
pubmed: 19844193 doi: 10.1038/mt.2009.248 issn: 1525-0016 issn: 1525-0024

Aurélie Goyenvalle, Arran Babbs, Dave Powell, Ryszard Kole, Sue Fletcher, Steve D Wilton, Kay E Davies