Antisense oligonucleotide therapy for spinocerebellar ataxia type 2
Nature (2017) - Comment
pubmed: 28405024  doi: 10.1038/nature22044  issn: 1476-4687  issn: 0028-0836 

Daniel R. Scoles, Pratap Meera, Matthew D. Schneider, Sharan Paul, Warunee Dansithong, Karla P. Figueroa, Gene Hung, Frank Rigo, C. Frank Bennett, Thomas S. Otis, Stefan M. Pulst