Development of a CRISPR/Cas9-based therapy for Hutchinson-Gilford progeria syndrome
Nature Medicine (2019) - Comments
pubmed: 30778239  doi: 10.1038/s41591-018-0338-6  issn: 1546-170x  issn: 1078-8956 

Olaya Santiago-Fernández, Fernando G. Osorio, Víctor Quesada, Francisco Rodríguez, Sammy Basso, Daniel Maeso, Loïc Rolas, Anna Barkaway, Sussan Nourshargh, Alicia R. Folgueras, José M. P. Freije, Carlos López-Otín