Correction of mucopolysaccharidosis type IIIb fibroblasts by lentiviral vector-mediated gene transfer
Biochemical Journal (2002) - Comments
pubmed: 12049639  doi: 10.1042/bj20011872  issn: 0264-6021  issn: 1470-8728 

Guglielmo R.D. Villani, Antonia Follenzi, Borghina Vanacore, Carmela Di Domenico, Luigi Naldini, Paola Di Natale