Multiplex CRISPR/Cas9-based genome editing for correction of dystrophin mutations that cause Duchenne muscular dystrophy
Nature Communications (2015) - Comments
pubmed: 25692716  doi: 10.1038/ncomms7244  issn: 2041-1723 

David G. Ousterout, Ami M. Kabadi, Pratiksha I. Thakore, William H. Majoros, Timothy E. Reddy, Charles A. Gersbach