Engineering multiple U7snRNA constructs to induce single and multiexon-skipping for Duchenne muscular dystrophy

Molecular Therapy (2012) - Comments
pubmed: 22354379 doi: 10.1038/mt.2012.26 issn: 1525-0024 issn: 1525-0016

Aurélie Goyenvalle, Jordan Wright, Arran Babbs, Vivienne Wilkins, Luis Garcia, Kay E Davies