Gene therapy for retinitis pigmentosa and Leber congenital amaurosis caused by defects in AIPL1: effective rescue of mouse models of partial and complete Aipl1 deficiency using AAV2/2 and AAV2/8 vectors
Human Molecular Genetics (2009) - Comments
pubmed: 19299492  doi: 10.1093/hmg/ddp133  issn: 1460-2083  issn: 0964-6906 

Mei Hong Tan, Alexander J. Smith, Basil Pawlyk, Xiaoyun Xu, Xiaoqing Liu, James B. Bainbridge, Mark Basche, Jenny McIntosh, Hoai Viet Tran, Amit Nathwani, Tiansen Li, Robin R. Ali